Presentation

Mutation-Independent Rhodopsin Gene Therapy by Knockdown and Replacement with a Single AAV Vector

BEST1 Gene Therapy Corrects a Diffuse Retina-Wide Microdetachment Modulated by Light Exposure

Bestrophinopathy: An RPE-Photoreceptor Interface Disease

Recombinant AAV-Mediated BEST1 Transfer to the Retinal Pigment Epithelium: Analysis of Serotype-Dependent Retinal Effects

Modeling the Structural Consequences of BEST1 Missense Mutations

Molecular Consequences of BEST1 Gene Mutations in Canine Multifocal Retinopathy Predict Functional Implications for Human Bestrophinopathies